We Must Accept Finite Disappointment, But Never Lose Infinite Hope

Spinal muscular atrophy is a genetic disorder of motor neurons, the cause of most forms of SMA is the deficiency of SMN protein. • full-length,functional SMN protein using genetic instructions carried in the SMN1 gene & identical neighboring gene, called SMN2, typically direct cells to produce a short, partially functional version of the SMN protein. • The great deal of SMA research is aimed at increasing SMN levels, improving muscle strength and function through development of various strategies